Pompe Disease Insights
Your patient and practitioner news, research and digital healthcare source
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This week's must-know community updates, latest research & events
Apply now: feature your voice in our cell and gene therapy series
Pompe Patient Becomes Ms. Wheelchair Alaska
NeurologyLive Brain Games: Pompe Disease Quiz
Navigating 8-Year Journey with Rare Genetic Disorder Diagnosis and Treatment
Italy Approves Reimbursement for New Treatments, Offering Hope to Rare Disease Patients
Gene Therapy Offers Hope for Pompe Disease in New Rat Study
New Treatment Shows Promise in Improving Muscle Function in Young Patients
Promising New Drug Overcomes ERT Limitations
Genes predict disease progression and Son's ear tube surgery hopes
Advancements in diagnosis and treatment offer hope for patients and families.
